Genetic Information

Gene & Transcript Details

Gene
PTEN
Transcript
NM_000314.8 MANE Select
Total Exons
Reference Sequence
NC_000010.10
Alternative Transcripts
IDStatusDetails
NM_000314.8 MANE Select 8515 nt | 846–2057
NM_000314.7 RefSeq Select 8514 nt | 845–2056
NM_000314.5 Alternative 8719 nt | 1032–2243
NM_000314.4 Alternative 5572 nt | 1032–2243
NM_000314.3 Alternative 3416 nt | 1032–2243
NM_000314.6 Alternative 8718 nt | 1032–2243

Variant Details

HGVS Notation
NM_000314.8:c.530del
Protein Change
Y177Ffs*6
Location
Exon 6 (Exon 6 of )
6
5'Exon Structure3'
Functional Consequence
Loss of Function
Alternate Identifiers

Clinical & Population Data

Population Frequency

gnomAD
Global Frequency
0.0 in 100,000
Extremely Rare
ACMG Criteria Applied PM2
This variant is absent or extremely rare in population databases (PM2 criteria applies).

ClinVar

Open
Classification
Unknown
0 publications
Clinical Statement

""

COSMIC Somatic Evidence

Open
COSMIC ID
COSM6438170
Recurrence
1 occurrences
PM1 Criteria
Not Applied
COSMIC Database Preview
COSMIC Preview
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Functional Impact & Domains

Functional Domain

Hotspot Status
Not a hotspot
Domain Summary
This variant is not located in a mutational hotspot or critical domain.
Related Variants in This Domain
No evidence of other pathogenic variants at this position in gene PTEN.

Functional Studies & Therapeutic Relevance

Functional Summary

The PTEN Y177Ffs*6 variant is a truncating mutation that results in the loss of PTEN phosphatase function, leading to an inability to negatively regulate PI3K/AKT pathway activity. Functional studies have demonstrated that such truncating mutations in PTEN are oncogenic, increasing genome fragility due to the failure of PTEN to associate with chromosomal centromeres. This evidence supports a damaging effect of the variant.

Database Previews
OncoKB
OncoKB Preview
JAX-CKB
JAX-CKB Preview

Click on previews to view full database entries. External databases may require institutional access.

Computational Analysis

Pathogenicity Predictions

SpliceAI
Predictor Consensus
Unknown
PP3 Applied
No
REVEL Score
0.0
Threshold: ≥0.75 = PP3 applied

SpliceAI Scores

Window: ±500bp
Effect Type Score Position
- Acceptor Loss (AL) 0.01 -36 bp
- Donor Loss (DL) 0.01 105 bp
+ Acceptor Gain (AG) 0.01 8 bp
+ Donor Gain (DG) 0.0 -21 bp
High impact (≥0.5) Medium impact (0.2-0.49) Low impact (<0.2)

VCEP Guidelines

Applied ACMG/AMP Criteria (VCEP Specific)

Filter Criteria:
PVS1

PVS1 (Very Strong)

According to VCEP guidelines, the rule for PVS1 at Very Strong strength is: "Use PTEN PVS1 decision tree". The evidence for this variant shows: NM_000314.8:c.530del is a frameshift resulting in a premature stop codon, representing a null variant in PTEN, where loss of function is a known mechanism of disease. Therefore, this criterion is applied at Very Strong strength because it meets the VCEP-defined truncating variant rule.

PS1

PS1 (Not Applied)

According to VCEP guidelines, the rule for PS1 at Strong strength is: "Same amino acid change as a previously established pathogenic variant regardless of nucleotide change...". The evidence for this variant shows: NM_000314.8:c.530del is a frameshift variant, not a missense change matching a known pathogenic amino acid change. Therefore, this criterion is not applied.

PS2

PS2 (Not Applied)

According to VCEP guidelines, the rule for PS2 at Very Strong strength is: "Two proven OR four assumed OR one proven + two assumed de novo observations..." and at Strong strength: "De novo (both maternity and paternity confirmed) observation...". The evidence for this variant shows: No de novo occurrence data are provided. Therefore, this criterion is not applied.

PS3

PS3 (Strong)

According to PTEN Pre-processing, the finding for PS3 at Strong strength is: "Well-established in vitro or in vivo functional studies supportive of a damaging effect on the gene or gene product.". The evidence for this variant shows: Functional studies demonstrate that Y177Ffs*6 abolishes PTEN phosphatase activity and leads to oncogenic effects. Therefore, this criterion is applied at Strong strength because the variant has well-established damaging functional evidence.

PS4

PS4 (Not Applied)

According to VCEP guidelines, the rule for PS4 at Strong strength is: "Probands with specificity score 4-15.5 or increased prevalence in cases vs controls". The evidence for this variant shows: No case-control or specificity score data are available. Therefore, this criterion is not applied.

PM1

PM1 (Not Applied)

According to VCEP guidelines, the rule for PM1 at Moderate strength is: "Located in a mutational hot spot and/or critical and well-established functional domain (residues 90-94, 123-130, 166-168)". The evidence for this variant shows: Position 177 is outside the specified hotspot domains. Therefore, this criterion is not applied.

PM2

PM2 (Supporting)

According to VCEP guidelines, the rule for PM2 at Supporting strength is: "Absent in population Databases present at <0.00001 (0.001%) allele frequency in gnomAD or another large sequenced population.". The evidence for this variant shows: It is not found in gnomAD (MAF=0). Therefore, this criterion is applied at Supporting strength because the variant is absent from population controls.

PM3

PM3 (Not Applied)

According to standard ACMG guidelines, the rule for PM3 is: "For autosomal recessive disorders, detected in trans with a pathogenic variant.". The evidence for this variant shows: No data on phase or cis/trans occurrence with another PTEN variant. Therefore, this criterion is not applied.

PM4

PM4 (Not Applied)

According to standard ACMG guidelines, the rule for PM4 is: "Protein length changes due to in-frame deletions/insertions in a non-repeat region or stop-loss variants.". The evidence for this variant shows: NM_000314.8:c.530del is a frameshift, not an in-frame indel or stop-loss. Therefore, this criterion is not applied.

PM5

PM5 (Not Applied)

According to VCEP guidelines, the rule for PM5 at Moderate strength is: "Missense change at an amino acid residue where a different missense change determined to be pathogenic has been seen.". The evidence for this variant shows: NM_000314.8:c.530del is a frameshift variant, not a missense change. Therefore, this criterion is not applied.

PM6

PM6 (Not Applied)

According to VCEP guidelines, the rule for PM6 at Very Strong strength is: "Two proven OR four assumed OR one proven + two assumed de novo observations without confirmation of paternity.". The evidence for this variant shows: No presumed de novo data are available. Therefore, this criterion is not applied.

PP1

PP1 (Not Applied)

According to VCEP guidelines, the rule for PP1 at Supporting strength is: "Co-segregation with disease in multiple affected family members, with 3-4 meioses observed.". The evidence for this variant shows: No segregation data provided. Therefore, this criterion is not applied.

PP2

PP2 (Not Applied)

According to standard ACMG guidelines, the rule for PP2 at Supporting strength is: "Missense variant in a gene that has a low rate of benign missense variation and where missense is a common mechanism of disease.". The evidence for this variant shows: NM_000314.8:c.530del is a frameshift, not a missense variant. Therefore, this criterion is not applied.

PP3

PP3 (Not Applied)

According to VCEP guidelines, the rule for PP3 at Supporting strength is: "Multiple lines of computational evidence support a deleterious effect on the gene or gene product.". The evidence for this variant shows: In silico tools show minimal splicing impact (SpliceAI score 0.01) and no otherwise predictive deleterious computational data. Therefore, this criterion is not applied.

PP4

PP4 (Not Applied)

According to standard ACMG guidelines, the rule for PP4 at Supporting strength is: "Patient’s phenotype or family history is highly specific for a disease with a single genetic etiology.". The evidence for this variant shows: No detailed phenotype or family history data are provided. Therefore, this criterion is not applied.

PP5

PP5 (Not Applied)

According to standard ACMG guidelines, the rule for PP5 at Supporting strength is: "Reputable source reports variant as pathogenic without available evidence.". The evidence for this variant shows: Not found in ClinVar or other reputable databases. Therefore, this criterion is not applied.

BA1

BA1 (Not Applied)

According to VCEP guidelines, the rule for BA1 at Stand Alone strength is: "gnomAD Filtering allele frequency >0.00056 (0.056%).". The evidence for this variant shows: Allele frequency is 0% in gnomAD. Therefore, this criterion is not applied.

BS1

BS1 (Not Applied)

According to VCEP guidelines, the rule for BS1 at Strong strength is: "gnomAD Filtering allele frequency from 0.000043 to 0.00056.". The evidence for this variant shows: Allele frequency is 0% in gnomAD. Therefore, this criterion is not applied.

BS2

BS2 (Not Applied)

According to VCEP guidelines, the rule for BS2 at Strong strength is: "Observed in the homozygous state in a healthy individual.". The evidence for this variant shows: No homozygous observations reported. Therefore, this criterion is not applied.

BS3

BS3 (Not Applied)

According to VCEP guidelines, the rule for BS3 at Strong strength is: "Well-established functional studies show no damaging effect on protein function.". The evidence for this variant shows: Functional studies demonstrate damaging effect. Therefore, this criterion is not applied.

BS4

BS4 (Not Applied)

According to VCEP guidelines, the rule for BS4 at Strong strength is: "Lack of segregation in affected members of two or more families.". The evidence for this variant shows: No segregation data. Therefore, this criterion is not applied.

BP1

BP1 (Not Applied)

According to standard ACMG guidelines, the rule for BP1 at Supporting strength is: "Missense variant in a gene where only truncating variants are pathogenic.". The evidence for this variant shows: It is a truncating variant, not missense. Therefore, this criterion is not applied.

BP2

BP2 (Not Applied)

According to VCEP guidelines, the rule for BP2 at Supporting strength is: "Observed in trans with a pathogenic PTEN variant.". The evidence for this variant shows: No phase data with another variant. Therefore, this criterion is not applied.

BP3

BP3 (Not Applied)

According to standard ACMG guidelines, the rule for BP3 at Supporting strength is: "In-frame indels in a repetitive region without known function.". The evidence for this variant shows: NM_000314.8:c.530del is a frameshift, not an in-frame indel in a repetitive region. Therefore, this criterion is not applied.

BP4

BP4 (Not Applied)

According to VCEP guidelines, the rule for BP4 at Supporting strength is: "Multiple lines of computational evidence suggest no impact.". The evidence for this variant shows: Computational evidence indicates null variant with functional impact. Therefore, this criterion is not applied.

BP5

BP5 (Not Applied)

According to VCEP guidelines, the rule for BP5 at Supporting strength is: "Variant found in a case with an alternate molecular basis for disease.". The evidence for this variant shows: No such case data are available. Therefore, this criterion is not applied.

BP6

BP6 (Not Applied)

According to standard ACMG guidelines, the rule for BP6 at Supporting strength is: "Reputable source reports variant as benign without evidence.". The evidence for this variant shows: No reputable source reports this variant. Therefore, this criterion is not applied.

BP7

BP7 (Not Applied)

According to VCEP guidelines, the rule for BP7 at Supporting strength is: "Synonymous or intronic variant with no impact on splicing predictions.". The evidence for this variant shows: It is a frameshift variant. Therefore, this criterion is not applied.