Genetic Information

Gene & Transcript Details

Gene
TP53
Transcript
NM_000546.6 MANE Select
Total Exons
Reference Sequence
NC_000017.10
Alternative Transcripts
IDStatusDetails
NM_000546.5 RefSeq Select 2591 nt | 203–1384
NM_000546.3 Alternative 2640 nt | 252–1433
NM_000546.6 MANE Select 2512 nt | 143–1324
NM_000546.4 Alternative 2586 nt | 198–1379
NM_000546.2 Alternative 2629 nt | 252–1433

Variant Details

HGVS Notation
NM_000546.6:c.309C>G
Protein Change
Y103*
Location
Exon 4 (Exon 4 of )
4
5'Exon Structure3'
Functional Consequence
Loss of Function
Alternate Identifiers

Clinical & Population Data

Population Frequency

gnomAD
Global Frequency
0.0 in 100,000
Extremely Rare
ACMG Criteria Applied PM2
This variant is absent or extremely rare in population databases (PM2 criteria applies).

ClinVar

Open
Classification
Pathogenic
1 publications
Publications List
PMID: 20522432

This sequence change creates a premature translational stop signal (p.Tyr103*) in the TP53 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in TP53 are known to be pathogenic (PMID: 20522432). This variant is not present in population databases (gnomAD no frequency). This premature translational stop signal has been observed in individual(s) with clinical features of Li-Fraumeni syndrome (PMID: 28681140). ClinVar contains an entry for this variant (Variation ID: 822878). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic.

Clinical Statement

"This variant has been reported in ClinVar as Pathogenic (5 clinical laboratories)."

COSMIC Somatic Evidence

Open
COSMIC ID
COSM44453
Recurrence
10 occurrences
PM1 Criteria
Not Applied
COSMIC Database Preview
COSMIC Preview
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Functional Impact & Domains

Functional Domain

Hotspot Status
Not a hotspot
Domain Summary
This variant is not located in a mutational hotspot or critical domain.
Related Variants in This Domain
No evidence of other pathogenic variants at this position in gene TP53.

Functional Studies & Therapeutic Relevance

Functional Summary

The TP53 Y103* variant is a truncating mutation that results in a premature stop codon, leading to the production of a truncated protein. Functional evidence indicates that truncating mutations in TP53 generally result in loss of protein function, promoting cancer cell proliferation, survival, and metastasis. Although Y103* has not been specifically biochemically characterized, it is predicted to be inactivating based on the effects of similar truncating mutations.

Database Previews
OncoKB
OncoKB Preview
JAX-CKB
JAX-CKB Preview

Click on previews to view full database entries. External databases may require institutional access.

Computational Analysis

Pathogenicity Predictions

SpliceAI
Predictor Consensus
Mixed/VUS
PP3 Applied
No
REVEL Score
0.0
Threshold: ≥0.75 = PP3 applied

SpliceAI Scores

Window: ±500bp
Effect Type Score Position
- Acceptor Loss (AL) 0.07 8 bp
- Donor Loss (DL) 0.01 -66 bp
+ Acceptor Gain (AG) 0.0 -1 bp
+ Donor Gain (DG) 0.08 134 bp
High impact (≥0.5) Medium impact (0.2-0.49) Low impact (<0.2)

VCEP Guidelines

Applied ACMG/AMP Criteria (VCEP Specific)

Filter Criteria:
PVS1

PVS1 (Very Strong)

According to VCEP guidelines: "Nonsense or frameshift variants predicted to undergo NMD (upstream of p.Lys351) apply PVS1 at Very Strong strength." The NM_000546.6:c.309C>G (p.Y103*) variant introduces a premature stop codon at amino acid 103, well upstream of p.Lys351, predicted to undergo NMD. Therefore, this criterion is applied at Very Strong strength.

PS1

PS1 (Not Applied)

According to VCEP guidelines: PS1 applies to variants resulting in the same amino acid change as a previously established TP53 pathogenic variant. The p.Y103* variant is a novel truncating change, not a reversion to a known pathogenic amino acid substitution. Therefore, PS1 is not applied.

PS2

PS2 (Not Applied)

According to VCEP guidelines: PS2 applies when confirmed de novo with parental testing. No de novo data are available for this variant. Therefore, PS2 is not applied.

PS3

PS3 (Not Applied)

According to VCEP caveat: "PS3 should not be applied at any strength if PVS1 is applied at full strength." PVS1 has been applied at Very Strong strength. Therefore, PS3 is not applied.

PS4

PS4 (Not Applied)

According to VCEP guidelines: PS4 requires statistically increased prevalence of variant in affected individuals. No case–control or proband point data are available. Therefore, PS4 is not applied.

PM1

PM1 (Not Applied)

According to VCEP guidelines: PM1 applies to germline missense variants at defined DNA-binding domain hotspots. p.Y103* is a truncating variant, not missense. Therefore, PM1 is not applied.

PM2

PM2 (Supporting)

According to VCEP guidelines: "PM2_Supporting: allele frequency <0.00003 in gnomAD or other large database." The variant is absent from gnomAD (MAF=0%). Therefore, PM2 is applied at Supporting strength.

PM3

PM3 (Not Applied)

According to standard ACMG: PM3 applies to recessive disorders with trans observations. TP53 disorders are dominant and no trans data exist. Therefore, PM3 is not applied.

PM4

PM4 (Not Applied)

According to standard ACMG: PM4 applies to protein length changes in in-frame indels or stop-loss. This is a stop-gain variant. Therefore, PM4 is not applied.

PM5

PM5 (Not Applied)

According to VCEP guidelines: PM5 applies to missense variants at residues with other pathogenic missense changes. p.Y103* is truncating, not missense. Therefore, PM5 is not applied.

PM6

PM6 (Not Applied)

According to VCEP guidelines: PM6 applies to assumed de novo without confirmation. No de novo information is available. Therefore, PM6 is not applied.

PP1

PP1 (Not Applied)

According to VCEP guidelines: PP1 applies when cosegregation is observed in families. No segregation data are provided. Therefore, PP1 is not applied.

PP2

PP2 (Not Applied)

According to standard ACMG: PP2 applies for missense in genes with low benign missense rate. p.Y103* is a truncating variant. Therefore, PP2 is not applied.

PP3

PP3 (Not Applied)

According to VCEP caveat: "PP3 should not be used in combination with PVS1." PVS1 is applied at full strength. Therefore, PP3 is not applied.

PP4

PP4 (Not Applied)

According to VCEP guidelines: PP4 applies when a specific phenotype is highly predictive for a gene. No phenotype data are provided. Therefore, PP4 is not applied.

PP5

PP5 (Supporting)

According to standard ACMG: "PP5: Reputable source recently reports variant as pathogenic, but the evidence is not available for independent evaluation." ClinVar lists this variant as Pathogenic by five laboratories. Therefore, PP5 is applied at Supporting strength.

BA1

BA1 (Not Applied)

According to VCEP guidelines: BA1 requires allele frequency ≥0.001. The variant is absent in population databases. Therefore, BA1 is not applied.

BS1

BS1 (Not Applied)

According to VCEP guidelines: BS1 applies for filtering AF ≥0.0003 but <0.001. The variant is absent. Therefore, BS1 is not applied.

BS2

BS2 (Not Applied)

According to VCEP guidelines: BS2 requires ≥8 unaffected older females. No such data. Therefore, BS2 is not applied.

BS3

BS3 (Not Applied)

According to VCEP guidelines: BS3 applies when functional assays show no loss of function. No such data. Therefore, BS3 is not applied.

BS4

BS4 (Not Applied)

According to VCEP guidelines: BS4 applies with lack of segregation in affected family members. No data available. Therefore, BS4 is not applied.

BP1

BP1 (Not Applied)

According to standard ACMG: BP1 applies to missense in gene where only truncating variants cause disease. p.Y103* is truncating, so BP1 is not applicable. Therefore, BP1 is not applied.

BP2

BP2 (Not Applied)

According to standard ACMG: BP2 applies when in trans with a pathogenic variant in dominant disorders. Not applicable. Therefore, BP2 is not applied.

BP3

BP3 (Not Applied)

According to standard ACMG: BP3 applies to in-frame indels in repetitive regions. Not applicable. Therefore, BP3 is not applied.

BP4

BP4 (Not Applied)

According to VCEP guidelines: BP4 applies to missense or splice predictions. p.Y103* is a stop-gain, so BP4 is not applied.

BP5

BP5 (Not Applied)

According to standard ACMG: BP5 applies when variant found in a case with an alternate molecular basis. No such data. Therefore, BP5 is not applied.

BP6

BP6 (Not Applied)

According to standard ACMG: BP6 applies to reputable source reporting benign without evidence. Not relevant. Therefore, BP6 is not applied.

BP7

BP7 (Not Applied)

According to VCEP guidelines: BP7 applies to silent or intronic variants with no splice impact. p.Y103* is coding nonsense. Therefore, BP7 is not applied.