Genetic Information

Gene & Transcript Details

Gene
PTEN
Transcript
NM_000314.8 MANE Select
Total Exons
Reference Sequence
NC_000010.10
Alternative Transcripts
IDStatusDetails
NM_000314.8 MANE Select 8515 nt | 846–2057
NM_000314.7 RefSeq Select 8514 nt | 845–2056
NM_000314.5 Alternative 8719 nt | 1032–2243
NM_000314.4 Alternative 5572 nt | 1032–2243
NM_000314.3 Alternative 3416 nt | 1032–2243
NM_000314.6 Alternative 8718 nt | 1032–2243

Variant Details

HGVS Notation
NM_000314.8:c.521_522del
Protein Change
Y174Cfs*5
Location
Exon 6 (Exon 6 of )
6
5'Exon Structure3'
Functional Consequence
Loss of Function
Alternate Identifiers

Clinical & Population Data

Population Frequency

gnomAD
Global Frequency
0.0 in 100,000
Extremely Rare
ACMG Criteria Applied PM2
This variant is absent or extremely rare in population databases (PM2 criteria applies).

ClinVar

Open
Classification
Unknown
0 publications
Clinical Statement

""

COSMIC Somatic Evidence

Open
COSMIC ID
Recurrence
0 occurrences
PM1 Criteria
Not Applied
COSMIC Database Preview
COSMIC Preview
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Functional Impact & Domains

Functional Domain

Hotspot Status
Not a hotspot
Domain Summary
This variant is not located in a mutational hotspot or critical domain.
Related Variants in This Domain
No evidence of other pathogenic variants at this position in gene PTEN.

Functional Studies & Therapeutic Relevance

Functional Summary

The PTEN Y174Cfs*5 variant is a truncating mutation that results in the loss of PTEN phosphatase function, leading to an inability to negatively regulate the PI3K/AKT pathway. Functional studies have shown that such truncating mutations are oncogenic, increasing genome fragility and disrupting chromosomal centromere association.

Database Previews
OncoKB
OncoKB Preview
JAX-CKB
JAX-CKB Preview

Click on previews to view full database entries. External databases may require institutional access.

Computational Analysis

Pathogenicity Predictions

SpliceAI
Predictor Consensus
Unknown
PP3 Applied
No
REVEL Score
0.0
Threshold: ≥0.75 = PP3 applied

SpliceAI Scores

Window: ±500bp
Effect Type Score Position
- Acceptor Loss (AL) 0.01 -26 bp
- Donor Loss (DL) 0.0 115 bp
+ Acceptor Gain (AG) 0.0 -9 bp
+ Donor Gain (DG) 0.0 119 bp
High impact (≥0.5) Medium impact (0.2-0.49) Low impact (<0.2)

VCEP Guidelines

Applied ACMG/AMP Criteria (VCEP Specific)

Filter Criteria:
PVS1

PVS1 (Very Strong)

According to VCEP guidelines, the rule for PVS1 is: "Very Strong Strength: Very Strong Use PTEN PVS1 decision tree." The evidence for this variant shows: a frameshift (Y174Cfs*5) predicted to result in loss of function in PTEN, a gene where LOF is a known mechanism of disease. Therefore, this criterion is applied at Very Strong strength because this is a null variant meeting the PTEN-specific PVS1 decision tree.

PS1

PS1 (Not Applied)

According to VCEP guidelines, the rule for PS1 is: "Strong: Same amino acid change as a previously established pathogenic variant regardless of nucleotide change..." The evidence for this variant shows: no previously established PTEN pathogenic variant with the same amino acid change. Therefore, this criterion is not applied.

PS2

PS2 (Not Applied)

According to VCEP guidelines, the rule for PS2 (Strong) is: "De novo (both maternity and paternity confirmed) in a patient with the disease and no family history." The evidence for this variant shows: de novo status not assessed. Therefore, this criterion is not applied.

PS3

PS3 (Strong)

According to VCEP guidelines, the rule for PS3 (Strong) is: "Well-established in vitro or in vivo functional studies supportive of a damaging effect on the gene or gene product." The evidence for this variant shows: studies demonstrate that Y174Cfs*5 abolishes PTEN phosphatase activity, dysregulates PI3K/AKT signaling, and is oncogenic. Therefore, this criterion is applied at Strong strength because robust functional data support a damaging effect.

PS4

PS4 (Not Applied)

According to VCEP guidelines, the rule for PS4 (Strong) is: "Prevalence of the variant in affected individuals is significantly increased compared with controls or specificity score 4–15.5." The evidence for this variant shows: no case–control or proband data. Therefore, this criterion is not applied.

PM1

PM1 (Not Applied)

According to VCEP guidelines, the rule for PM1 (Moderate) is: "Located in a mutational hot spot and/or critical and well-established functional domain including residues 90–94, 123–130, 166–168." The evidence for this variant shows: position Y174 is outside the defined catalytic motifs. Therefore, this criterion is not applied.

PM2

PM2 (Supporting)

According to VCEP guidelines, the rule for PM2 is: "Supporting Strength: Supporting Absent in population Databases present at <0.00001 allele frequency in gnomAD." The evidence for this variant shows: MAF = 0% in gnomAD. Therefore, this criterion is applied at Supporting strength because the variant is absent from controls.

PM3

PM3 (Not Applied)

According to standard ACMG guidelines, the rule for PM3 is: "For recessive disorders, detected in trans with a pathogenic variant." The evidence for this variant shows: no data on allelic configuration. Therefore, this criterion is not applied.

PM4

PM4 (Not Applied)

According to VCEP guidelines, the rule for PM4 (Moderate) is: "Protein length changes due to in-frame insertions/deletions in a non-repeat region or stop-loss variants." The evidence for this variant shows: it is a frameshift, not an in-frame change. Therefore, this criterion is not applied.

PM5

PM5 (Not Applied)

According to VCEP guidelines, the rule for PM5 (Moderate) is: "Missense change at a residue where a different missense change is pathogenic." The evidence for this variant shows: it is a frameshift, not a missense change. Therefore, this criterion is not applied.

PM6

PM6 (Not Applied)

According to VCEP guidelines, the rule for PM6 (Strong) is: "Two probands with presumed de novo occurrence without confirmation." The evidence for this variant shows: no de novo data available. Therefore, this criterion is not applied.

PP1

PP1 (Not Applied)

According to VCEP guidelines, the rule for PP1 (Supporting) is: "Co-segregation with disease in multiple affected family members (3–4 meioses)." The evidence for this variant shows: no segregation data. Therefore, this criterion is not applied.

PP2

PP2 (Not Applied)

According to VCEP guidelines, the rule for PP2 (Supporting) is: "Missense variant in a gene with low benign missense rate where missense is a common mechanism." The evidence for this variant shows: it is a frameshift. Therefore, this criterion is not applied.

PP3

PP3 (Not Applied)

According to VCEP guidelines, the rule for PP3 (Supporting) is: "Multiple lines of computational evidence support deleterious effect (REVEL>0.7 for missense)." The evidence for this variant shows: insufficient in silico data for splicing or missense. Therefore, this criterion is not applied.

PP4

PP4 (Not Applied)

According to standard ACMG guidelines, the rule for PP4 is: "Phenotype highly specific for a disease with a single genetic etiology." The evidence for this variant shows: no patient phenotype provided. Therefore, this criterion is not applied.

PP5

PP5 (Not Applied)

According to standard ACMG guidelines, the rule for PP5 is: "Reputable source reports variant as pathogenic without available evidence." The evidence for this variant shows: no such report. Therefore, this criterion is not applied.

BA1

BA1 (Not Applied)

According to VCEP guidelines, the rule for BA1 is: "Stand Alone: gnomAD filtering allele frequency >0.00056." The evidence for this variant shows: MAF = 0%. Therefore, this criterion is not applied.

BS1

BS1 (Not Applied)

According to VCEP guidelines, the rule for BS1 (Strong) is: "Allele frequency from 0.000043 up to 0.00056." The evidence for this variant shows: MAF = 0%. Therefore, this criterion is not applied.

BS2

BS2 (Not Applied)

According to VCEP guidelines, the rule for BS2 (Strong) is: "Observed in homozygous state in healthy individual." The evidence for this variant shows: no such observations. Therefore, this criterion is not applied.

BS3

BS3 (Not Applied)

According to VCEP guidelines, the rule for BS3 (Strong) is: "Well-established functional studies show no damaging effect." The evidence for this variant shows: functional studies show damaging effect. Therefore, this criterion is not applied.

BS4

BS4 (Not Applied)

According to VCEP guidelines, the rule for BS4 (Strong) is: "Lack of segregation in affected members of two families." The evidence for this variant shows: no segregation data. Therefore, this criterion is not applied.

BP1

BP1 (Not Applied)

According to standard ACMG guidelines, the rule for BP1 is: "Missense variant in gene where only truncating variants cause disease." The evidence for this variant shows: it is truncating. Therefore, this criterion is not applied.

BP2

BP2 (Not Applied)

According to VCEP guidelines, the rule for BP2 (Supporting) is: "Observed in trans with a pathogenic PTEN variant." The evidence for this variant shows: no data on allelic phase. Therefore, this criterion is not applied.

BP3

BP3 (Not Applied)

According to standard ACMG guidelines, the rule for BP3 is: "In-frame insertion/deletion in a repetitive region without functional impact." The evidence for this variant shows: frameshift outside repeat region. Therefore, this criterion is not applied.

BP4

BP4 (Not Applied)

According to VCEP guidelines, the rule for BP4 (Supporting) is: "Multiple lines of computational evidence suggest no impact." The evidence for this variant shows: no computational support for benign effect. Therefore, this criterion is not applied.

BP5

BP5 (Not Applied)

According to VCEP guidelines, the rule for BP5 (Supporting) is: "Variant found in case with alternate molecular basis for disease." The evidence for this variant shows: no such alternate basis. Therefore, this criterion is not applied.

BP6

BP6 (Not Applied)

According to standard ACMG guidelines, the rule for BP6 is: "Reputable source reports variant as benign without evidence." The evidence for this variant shows: no such report. Therefore, this criterion is not applied.

BP7

BP7 (Not Applied)

According to VCEP guidelines, the rule for BP7 (Supporting) is: "Synonymous or intronic variant with no splicing impact predicted." The evidence for this variant shows: it is a frameshift. Therefore, this criterion is not applied.