Genetic Information

Gene & Transcript Details

Gene
PIK3CA
Transcript
NM_006218.4 MANE Select
Total Exons
Reference Sequence
NC_000003.11
Alternative Transcripts
IDStatusDetails
NM_006218.2 Alternative 3724 nt | 158–3364
NM_006218.3 Alternative 9104 nt | 158–3364
NM_006218.4 MANE Select 9259 nt | 324–3530

Variant Details

HGVS Notation
NM_006218.4:c.1132T>C
Protein Change
C378R
Location
Exon 6 (Exon 6 of )
6
5'Exon Structure3'
Functional Consequence
Loss of Function
Alternate Identifiers

Clinical & Population Data

Population Frequency

gnomAD
Global Frequency
0.0 in 100,000
Extremely Rare
ACMG Criteria Applied PM2
This variant is absent or extremely rare in population databases (PM2 criteria applies).

ClinVar

Open
Classification
Likely Pathogenic
2 publications
Publications List
PMID: 30270358

The c.1132T>C (p.C378R) alteration is located in exon 6 (coding exon 5) of the PIK3CA gene. This alteration results from a T to C substitution at nucleotide position 1132, causing the cysteine (C) at amino acid position 378 to be replaced by an arginine (R). This variant was not reported in population-based cohorts in the Genome Aggregation Database (gnomAD). This variant has been identified as a confirmed or suspected result of somatic mosaicism in affected tissue samples from individual(s) with vascular malformations, limb and/or digital anomalies, and adipose overgrowth; all features consistent with PIK3CA-related disorder (Parker, 2019; Delgado-Miguel, 2021; Paolacci, 2020; Su, 2022; Zerbib, 2024; McNulty, 2019). In at least one individual, it was determined to be de novo (Lunke, 2023). This amino acid position is highly conserved in available vertebrate species. This alteration is predicted to be deleterious by in silico analysis. Based on the available evidence, this alteration is classified as pathogenic.

Clinical Statement

"This variant has been reported in ClinVar as Likely pathogenic (1 clinical laboratories) and as Pathogenic (4 clinical laboratories)."

COSMIC Somatic Evidence

Open
COSMIC ID
COSM1041477
Recurrence
16 occurrences
PM1 Criteria
Not Applied
COSMIC Database Preview
COSMIC Preview
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Functional Impact & Domains

Functional Domain

Hotspot Status
Not a hotspot
Domain Summary
This variant is not located in a mutational hotspot or critical domain.
Related Variants in This Domain
No evidence of other pathogenic variants at this position in gene PIK3CA.

Functional Studies & Therapeutic Relevance

Functional Summary

Error in OpenAI Consolidation. OncoKB: PIK3CAC378RPIK3CAC378RSomaticNCBI Gene:5290|Show additional gene information Variant OverviewPIK3CA, the catalytic subunit of PI3-kinase, is frequently mutated in a diverse range of cancers including breast, endometrial and cervical cancers.The PIK3CA C378R mutation is likely oncogenic.Hide mutation effect description The PIK3CA C378R mutation is located in the C2 domain in exon 6 of the protein. This mutation has been found in colon cancer (PMID: 17363507). A colon cancer cell line with this mutation displayed increased PI3K enzyme activity, increased activation of downstream PI3K targets and resistance to apoptosis compared to cancer cells with wildtype PIK3CA (PMID: 17363507). JAX-CKB: PIK3CA C378R lies within the C2 PI3K-type domain of the Pik3ca protein (UniProt.org). C378R results in constitutive activation of Pi3k and Akt signaling, and decreased apoptosis in cell culture (PMID: 17363507).

Database Previews
OncoKB
OncoKB Preview
JAX-CKB
JAX-CKB Preview

Click on previews to view full database entries. External databases may require institutional access.

Computational Analysis

Pathogenicity Predictions

SpliceAI
Predictor Consensus
Mixed/VUS
PP3 Applied
No
REVEL Score
0.0
Threshold: ≥0.75 = PP3 applied

SpliceAI Scores

Window: ±500bp
Effect Type Score Position
- Acceptor Loss (AL) 0.0 156 bp
- Donor Loss (DL) 0.0 -57 bp
+ Acceptor Gain (AG) 0.0 -56 bp
+ Donor Gain (DG) 0.0 -383 bp
High impact (≥0.5) Medium impact (0.2-0.49) Low impact (<0.2)

VCEP Guidelines

Applied ACMG/AMP Criteria (VCEP Specific)

Filter Criteria:
PS3

PS3 (Unknown (Pre-LLM))

From pre-LLM assessment (LLM Failed)

PM2

PM2 (Unknown (Pre-LLM))

From pre-LLM assessment (LLM Failed)

PP5

PP5 (Unknown (Pre-LLM))

From pre-LLM assessment (LLM Failed)

BP4

BP4 (Unknown (Pre-LLM))

From pre-LLM assessment (LLM Failed)